Researchers liken the Huntington’s disease Integrated Staging System (HD-ISS) to the system currently used to stage cancer.
“We recognize the urgent need for new treatments that can both improve and extend the lives of people diagnosed with these diseases.”
One-year clinical trial results show a deceleration in functional decline that is similar, but “more pronounced” than the previously reported 6-...
"These data illustrate how mechanistic precision in treatment design can help patients gain benefit from their regimen regardless of the genetic...
After 12 months of risdiplam treatment, the majority of presymptomatic infants with SMA reached key motor milestones.
Compared with the IV formation of the drug, the oral form has been shown to generate comparable levels of active drug in the bloodstream.
These are the first guidelines on how to manage adult and pediatric patients with idiopathic inflammatory myopathies (IIM).
Nearly all individuals who developed GBS after the Janssen vaccine had facial weakness or paralysis, in addition to weakness and decreased...
“Four years later, his patients were still shocked about what happened and couldn’t reconcile the person they knew with the event that happened...
Red blood cells infused with dexamethasone sodium phosphate delayed symptom progression and improved survival.
From the Journals
Patients with restless legs syndrome showed less brain demyelination than those without RLS.